Insights
Evidence, briefs and structural thinking on rare disease.
White papers and strategic briefs on the clinical, regulatory and data infrastructure of rare disease.
Featured strategic brief
Bringing Small Molecules to Life
A structural view of how rare disease small molecules can be translated across the Boston–Brazil corridor.
Editorial pillars
What we write about.
01
Rare disease infrastructure
How the pathway from molecule to patient is actually assembled.
02
Brazil as a clinical environment
Regulatory, institutional and cohort perspectives.
03
Data & bioinformatics
Evidence, governance and platform design.
04
Boston ↔ Brazil corridor
Translation between two of the world's rare disease ecosystems.
05
Access & real-world evidence
Reimbursement, continuity, longitudinal data.
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Occasional writing for developers, investigators and investors working in rare disease.
Pharma²⁸
Building rare disease infrastructure, together.
If you are advancing a therapy, investing in the space, running a clinical program or coordinating patient identification — start a conversation with us.